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Highlights:
Statistically significant improvement from baseline assessed by both clinicians and caregivers in all four efficacy measures specifically designed for Pitt Hopkins syndrome (Wilcoxon signed rank test p<0.05) Clinician and caregiver global efficacy measures showed a level of improvement considered clinically meaningful:
- Clinical Global Impression of Improvement (CGI-I) - mean score of 2.6, with 9 out of 11 children showing improvement assessed by clinicians - Caregiver Overall Imp...
>>> Read more: Neuren Phase 2 trial shows significant improvements in Pitt Hopkins syndrome
Statistically significant improvement from baseline assessed by both clinicians and caregivers in all four efficacy measures specifically designed for Pitt Hopkins syndrome (Wilcoxon signed rank test p<0.05) Clinician and caregiver global efficacy measures showed a level of improvement considered clinically meaningful:
- Clinical Global Impression of Improvement (CGI-I) - mean score of 2.6, with 9 out of 11 children showing improvement assessed by clinicians - Caregiver Overall Imp...
>>> Read more: Neuren Phase 2 trial shows significant improvements in Pitt Hopkins syndrome
